Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ... Science 341 (6148), 1233151, 2013 | 1223 | 2013 |
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors D Pellin, M Loperfido, C Baricordi, SL Wolock, A Montepeloso, ... Nature communications 10 (1), 2395, 2019 | 287 | 2019 |
In vivo tracking of human hematopoiesis reveals patterns of clonal dynamics during early and steady-state reconstitution phases L Biasco, D Pellin, S Scala, F Dionisio, L Basso-Ricci, L Leonardelli, ... Cell stem cell 19 (1), 107-119, 2016 | 250 | 2016 |
High-definition mapping of retroviral integration sites identifies active regulatory elements in human multipotent hematopoietic progenitors C Cattoglio, D Pellin, E Rizzi, G Maruggi, G Corti, F Miselli, D Sartori, ... Blood, The Journal of the American Society of Hematology 116 (25), 5507-5517, 2010 | 197 | 2010 |
Adaptation of Pseudomonas aeruginosa in Cystic Fibrosis Airways Influences Virulence of Staphylococcus aureus In Vitro and Murine Models of Co-Infection R Baldan, C Cigana, F Testa, I Bianconi, M De Simone, D Pellin, ... PloS one 9 (3), e89614, 2014 | 192 | 2014 |
Chromatin organization at the nuclear pore favours HIV replication M Lelek, N Casartelli, D Pellin, E Rizzi, P Souque, M Severgnini, ... Nature communications 6 (1), 6483, 2015 | 143 | 2015 |
Integration profile of retroviral vector in gene therapy treated patients is cell‐specific according to gene expression and chromatin conformation of target cell L Biasco, A Ambrosi, D Pellin, C Bartholomae, I Brigida, MG Roncarolo, ... EMBO Molecular Medicine 3 (2), 89-101, 2011 | 126 | 2011 |
Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans S Scala, L Basso-Ricci, F Dionisio, D Pellin, S Giannelli, FA Salerio, ... Nature medicine 24 (11), 1683-1690, 2018 | 110 | 2018 |
Genome-wide discovery of small RNAs in Mycobacterium tuberculosis P Miotto, F Forti, A Ambrosi, D Pellin, DF Veiga, G Balazsi, ML Gennaro, ... PLoS one 7 (12), e51950, 2012 | 98 | 2012 |
A genome-wide identification analysis of small regulatory RNAs in Mycobacterium tuberculosis by RNA-Seq and conservation analysis D Pellin, P Miotto, A Ambrosi, DM Cirillo, C Di Serio PloS one 7 (3), e32723, 2012 | 62 | 2012 |
BCL11A enhancer–edited hematopoietic stem cells persist in rhesus monkeys without toxicity S Demirci, J Zeng, Y Wu, N Uchida, AH Shen, D Pellin, J Gamer, ... The Journal of clinical investigation 130 (12), 6677-6687, 2020 | 56 | 2020 |
High-definition mapping of retroviral integration sites defines the fate of allogeneic T cells after donor lymphocyte infusion C Cattoglio, G Maruggi, C Bartholomae, N Malani, D Pellin, ... PLoS One 5 (12), e15688, 2010 | 56 | 2010 |
Preclinical evaluation of a novel lentiviral vector driving lineage-specific BCL11A knockdown for sickle cell gene therapy C Brendel, O Negre, M Rothe, S Guda, G Parsons, C Harris, ... Molecular Therapy-Methods & Clinical Development 17, 589-600, 2020 | 49 | 2020 |
CRISPR-SURF: discovering regulatory elements by deconvolution of CRISPR tiling screen data JY Hsu, CP Fulco, MA Cole, MC Canver, D Pellin, F Sher, R Farouni, ... Nature methods 15 (12), 992-993, 2018 | 34 | 2018 |
Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors A Moiani, A Miccio, E Rizzi, M Severgnini, D Pellin, JD Suerth, C Baum, ... PLoS One 8 (1), e55721, 2013 | 24 | 2013 |
Epitope editing enables targeted immunotherapy of acute myeloid leukaemia G Casirati, A Cosentino, A Mucci, M Salah Mahmoud, I Ugarte Zabala, ... Nature 621 (7978), 404-414, 2023 | 20 | 2023 |
Estimated comparative integration hotspots identify different behaviors of retroviral gene transfer vectors A Ambrosi, IK Glad, D Pellin, C Cattoglio, F Mavilio, C Di Serio, A Frigessi PLoS Computational Biology 7 (12), e1002292, 2011 | 19 | 2011 |
Lentivirus-based gene therapy of hematopoietic stem cells in Wiskott-Aldrich syndrome A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ... Science (New York, NY) 341 (6148), 1233151, 2013 | 18 | 2013 |
Penalized inference of the hematopoietic cell differentiation network via high-dimensional clonal tracking D Pellin, L Biasco, A Aiuti, MC Di Serio, EC Wit Applied Network Science 4 (1), 1-26, 2019 | 10 | 2019 |
Meeting FDA Guidance recommendations for replication-competent virus and insertional oncogenesis testing K Cornetta, TY Lin, D Pellin, DB Kohn Molecular Therapy Methods & Clinical Development 28, 28-39, 2023 | 8 | 2023 |